On January 30, 2025, a group of thoracic oncologists gathered for an in-person workshop to discuss advances in diagnosing and treating non–small cell lung cancer (NSCLC) related to an HER2 mutation. The session was moderated by Joshua Sabari, MD; and Benjamin Levy, MD. As they focused on HER2 biomarker testing, treatment sequencing, and emerging therapies (including antibody-drug conjugates [ADCs] and TKIs), the faculty reviewed clinical trial data, shared real-world experiences, and debated evolving treatment strategies.
Session Overview & Highlights
Diagnosing HER2-Mutant NSCLC
Faculty emphasized the importance of comprehensive molecular testing using both tissue and liquid biopsy to ensure that HER2 mutations are not missed. Adoption of next-generation sequencing (NGS) varies across institutions with some using in-house panels and others relying on commercial assays like Caris, Foundation, or Tempus. HER2 immunohistochemistry (IHC) testing remains inconsistent due to limited tissue availability and financial barriers. Many patients seeking a second opinion lack full NGS results upon referral, which delays optimal treatment selection.
ADCs in HER2-Mutant NSCLC
Trastuzumab deruxtecan (T-DXd) is the preferred second-line treatment per NCCN and FDA guidelines; its frontline potential is being evaluated in HERTHENA-Lung04. Faculty reviewed data from the DESTINY-Lung01, DESTINY-Lung02, and DESTINY-PanTumor02 trials that continue to shape the role of T-DXd in treatment sequencing. Interstitial lung disease (ILD) remains a concern that requires early monitoring and steroid intervention for patients on T-DXd. Central nervous system (CNS) efficacy is uncertain, with some faculty reporting intracranial responses and others observing progression of brain disease. Toxicities including fatigue and ILD are common; cardiotoxicity, however, appears to be minimal, leading to questions about the necessity of routine echocardiography. A key debate emerged over whether T-DXd functions more as targeted therapy or chemotherapy given its mechanism of action and toxicity profile.
HER2-Targeted TKIs: Emerging Options
The use of HER2-targeted TKIs, particularly zongertinib, is gaining traction. When compared with previous TKIs (eg, poziotinib), zongertinib demonstrates high selectivity and tolerability. Faculty reviewed Beamion LUNG-1 data and discussed the ongoing Beamion LUNG-2 trial, evaluating zongertinib’s efficacy compared to chemotherapy. Poziotinib therapy failed due to toxicity despite promising early response rates. Zongertinib avoids wild-type EGFR inhibition, reducing the toxicity seen with previous TKIs. CNS efficacy remains a key concern, as patients with HER2-mutant disease frequently develop brain metastases. Other HER2-targeted TKIs (eg, VAL-330, Enliven-002, Iambic-001) are in development with a focus on CNS activity and durability. Faculty debated the place of zongertinib in treatment sequencing; some favored first-line use due to oral administration and tolerability, whereas others preferred to use it after T-DXd.
Discussion Themes and Expert Insights
HER2-mutant NSCLC appears less responsive to chemotherapy, which raises concerns about the use of chemotherapy-immunotherapy regimens in this setting. Financial barriers continue to impact treatment choices, particularly for HER2 IHC 2+ patients, who currently do not qualify for T-DXd under existing guidelines.
The future of HER2-mutant NSCLC treatment will likely involve combination approaches that incorporate ADCs, TKIs, and bispecific antibodies and focus on sequencing strategies to improve durability of response. Faculty emphasized the need to study resistance mechanisms, as a better understanding of HER2-driven pathways could guide more effective treatment strategies.
Unmet Needs and Recommendations
Standardized HER2 testing is critical for reducing missed diagnoses and ensuring timely treatment selection. Given the high rate of CNS metastases, HER2-targeted therapies must demonstrate strong intracranial activity to prevent disease progression.
Faculty debated whether TKIs like zongertinib should replace ADCs in the frontline setting, emphasizing the need for further clinical validation. Future research should focus on combination strategies (eg, ADCs plus TKIs, chemotherapy combinations, or novel targeted agents) to improve treatment durability.
Finally, payer coverage and reimbursement policies must evolve along with treatment advances to ensure broad patient access to new HER2-targeted therapies.
Conclusion
The treatment landscape for NSCLC related to HER2 mutation is evolving rapidly, and ongoing clinical trials are poised to reshape frontline therapy. While T-DXd remains the preferred second-line option, HER2-targeted TKIs like zongertinib are gaining attention due to oral convenience and lower toxicity.
Faculty agreed that treatment sequencing, CNS activity, and combination approaches must be carefully considered moving forward. With multiple novel therapies in development, the coming years are expected to redefine HER2-mutant NSCLC treatment paradigms and provide new hope for patients with this rare but challenging disease.
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